Gene, Cell, and Molecular Therapies

Catalog description

Credits 3. 3 Lecture Hours. Introduction to types of therapies including gene replacement, exon skipping, stop codon readthrough, gene editing, and stem cell therapy; use of monogenic, neuromuscular disorders for the application of these types of treatments; basic principles of gene, cell, and molecular therapy and the application to research projects, where applicable; presentation of peer-reviewed journal articles pertaining to the course content. Prerequisites: Graduate classification.