Gene Therapy: Curing the Incurable

Catalog description

This course focuses on the principles of gene therapy for disease treatment or drug delivery. Technical aspects associated with the development of the therapeutic approach will be covered along with the concepts related to the legal, ethical, economic, religious, and philosophical consequences of implementing gene-editing technologies for common and rare (often childhood) diseases. The "agora" will define ethical considerations of risk/benefit, informed consent, priority therapy targets, optimal technologies and delivery, costs, FDA regulation, and desired outcomes across disciplines.This course will be available to all students at CWRU, with consent of instructor. Students must have a foundational understanding in cell biology, exposure to regenerative medicine and genetics. Recommended Preparation: RGME 535 or RGME 525 .